QUESTION IMAGE
Question
which disorder has been treated by ex vivo gene therapy?
a ada deficiency
b aids
c cystic fibrosis
d all of the above
Ex vivo gene therapy involves modifying cells outside the body and then reintroducing them. ADA (Adenosine Deaminase) deficiency was one of the first disorders treated with ex vivo gene therapy, where lymphocytes were genetically modified. AIDS and cystic fibrosis have different treatment approaches for gene therapy (with cystic fibrosis more associated with in vivo approaches in some cases, and AIDS not primarily treated with ex vivo gene therapy as a standard). So the correct option is a.
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a. ADA deficiency